题名 | Safety and efficacy of apitegromab in nonambulatory type 2 or type 3 spinal muscular atrophy (SAPPHIRE): a phase 3, double-blind, randomised, placebo-controlled trial |
链接 | https://www.thelancet.com/journals/laneur/article/PIIS1474-4422(25)00225-X/abstract |
https://www.thelancet.com/journals/laneur/article/PIIS1474-4422(25)00225-X/abstract
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